Ompenaclid (RGX-202-01) is an orally active inhibitor of SLC6A8 transport protein. Ompenaclid (RGX-202-01) strongly inhibits creatine import in vitro and in vivo, decreases intracellular phosphocreatine and ATP levels, and induces apoptosis. Ompenaclid (RGX-202-01) has been used in oncology and Duchenne muscular dystrophy studies.
Molekulargewicht:
131.13
Reinheit:
>98.0%
CAS Nummer:
[353-09-3]
Formel:
C4H9N3O2
Target-Kategorie:
Metabolite/Endogenous Metabolite
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