Viltolarsen (NS-065/NCNP-01) is a phosphorodiamidate morpholino antisense oligonucleotide. Viltolarsen binds to exon 53 of the dystrophin mRNA precursor and restores the amino acid open-reading frame by skipping exon 53, resulting in the production of a shortened dystrophin protein that contains essential functional portions. Viltolarsen has the potential for Duchenne muscular dystrophy (DMD) research[1][2].
Molekulargewicht:
6924.80
Reinheit:
95.25
CAS Nummer:
[2055732-84-6]
Formel:
C244H381N113O88P20
Target-Kategorie:
Dystrophin,Nucleoside Antimetabolite/Analog
Anwendungsbeschreibung:
Oligonucleotides
* Mehrwertsteuer und Versandkosten nicht enthalten. Irrtümer und Preisänderungen vorbehalten