Afegostat is an acid beta-glucosidase (GCase) active site inhibitor that acts as a pharmacological chaperone. Afegostat inhibits GCase with K(i) ~30 nM for wild-type and mutant enzymes. Afegostat was an experimental drug for the treatment of certain forms of Gauchers disease.
Molekulargewicht:
183.63
CAS Nummer:
[161302-93-8]
Formel:
C6H14ClNO3
Target-Kategorie:
Others|||glycosidase
T23653
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