Olezarsen is an N-acetyl-galactosamine-conjugated antisense oligonucleotide that selectively targets hepatic APOC3 messenger RNA to inhibit apolipoprotein C-III production, resulting in significant triglyceride lowering and providing a precision medicine research platform for metabolic disorders and cardiovascular disease risk reduction.
Molekulargewicht:
8684.86
CAS Nummer:
[2097587-83-0]
Target-Kategorie:
Others
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