PTC258 is a specific, orally active modulator of the splicing of the Elongator complex protein 1 gene (ELP1), enhancing its expression both in vitro and in vivo. Additionally, PTC258 has demonstrated good tolerability in a mouse model [1].
Molecular Weight:
351.92
CAS Number:
[2476724-74-8]
Formula:
C16H18ClN3S2
Target:
Others|||DNA/RNA Synthesis
T81355
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